Usher Syndrome Ireland
Usher Syndrome Ireland
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    • Home
    • Information
      • What is Usher Syndrome?
      • Usher Syndrome - Genetics
      • Adults - Newly Diagnosed?
      • Adults - USH Community
      • Newly Diagnosed Child?
      • Telling Your Child
      • Parents - USH Community
      • USH Connect
    • HCPs
      • Information for HCPs
      • Overview - Usher Syndrome
      • Create Accessibility
      • Talks/Presentations
    • Research
      • Usher Syndrome Research
      • Understanding USHResearch
      • USH Patient Registries
      • USH Research News
    • More Info & Resources
      • Usher Syndrome Leaflets
      • Yellow Sticker Campaign
      • Life with USH - Blog
      • Help & Resources
      • Archived Newsletters
    • About Us
      • About Us
      • Meet Our Team
      • Contact Us
    • Support Us
      • Support Us
      • Donate Today
    • Q&A with Jeremy
  • Home
  • Information
    • What is Usher Syndrome?
    • Usher Syndrome - Genetics
    • Adults - Newly Diagnosed?
    • Adults - USH Community
    • Newly Diagnosed Child?
    • Telling Your Child
    • Parents - USH Community
    • USH Connect
  • HCPs
    • Information for HCPs
    • Overview - Usher Syndrome
    • Create Accessibility
    • Talks/Presentations
  • Research
    • Usher Syndrome Research
    • Understanding USHResearch
    • USH Patient Registries
    • USH Research News
  • More Info & Resources
    • Usher Syndrome Leaflets
    • Yellow Sticker Campaign
    • Life with USH - Blog
    • Help & Resources
    • Archived Newsletters
  • About Us
    • About Us
    • Meet Our Team
    • Contact Us
  • Support Us
    • Support Us
    • Donate Today
  • Q&A with Jeremy

Eye on the Research

Antisense Oligonucleotide (AON)

A list of AON study/studies currently underway that may benefit patients with Usher syndrome. Please refer to the link under each trial for more information on that trial. Please be aware, all information provided are for informational purposes only, and are in no way endorsed or approved by Usher Syndrome Ireland. 


Phase 2/3 Clinical Trial


  • ProQR trial Sirius investigates whether the RNA therapy Ultevursen (previously known as QR-421), using antisense oligonucleotide technology, is effective and safe for the treatment of retinitis pigmentosa due to USH2A exon 13 mutations. Based on previous positive results from phase 1/2 Stellar trial, ProQR has now begun this next phase. More information can be found here: https://www.proqr.com/QR-421a-for-USH2A-RP

 << Click here to return to  'Understanding USH Research'  


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Address

15 Windsor Terrace, 

Dun Laoghaire, Co. Dublin, 

A96 RF29


Reg. Number: 688621 

Reg Charity Number: 20206288


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