Eye on the Research

---

A list of AON trial(s) currently underway that may benefit patients with Usher syndrome. Please refer to the link under each trial for more information on that trial. Please be aware that all information provided are for informational purposes only, and are in no way endorsed or approved by Usher Syndrome Ireland. 

Phase 2 

• ProQR trial Stellar investigates whether the RNA therapy QR-421, an antisense oligonucleotide, for the treatment of retinitis pigmentosa due to USH2A exon 13 mutations is effective and safe. Based on previous positive results from Stellar, ProQR plan to begin two final stage Phase 2/3 clinical trials called Sirius and Celeste at the end of 2021. More information can be found here: https://www.proqr.com/Stellar-study-for-USH2A-retinitis-pigmentosa 

 << Click here to return to  'Understanding the Research'