Eye on the Research

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A list of AON study/studies currently underway that may benefit patients with Usher syndrome. Please refer to the link under each trial for more information on that trial. Please be aware, all information provided are for informational purposes only, and are in no way endorsed or approved by Usher Syndrome Ireland. 

Phase 2/3 Clinical Trial

• ProQR trial Sirius investigates whether the RNA therapy Ultevursen (previously known as QR-421), using antisense oligonucleotide technology, is effective and safe for the treatment of retinitis pigmentosa due to USH2A exon 13 mutations. Based on previous positive results from phase 1/2 Stellar trial, ProQR has now begun this next phase. More information can be found here: https://www.proqr.com/QR-421a-for-USH2A-RP